The Sanfilippo Children's Foundation is thrilled to announce that the Australian arm of the Abeona Therapeutics gene therapy clinical trial for Sanfilippo Type A has been granted regulatory approval by the Government’s Therapeutics Goods Administration (TGA). The trial will take place at the Women's and Children's Hospital in Adelaide. [...]
While TGA approval is exciting news, please be mindful that it’s also an incredibly nerve-wracking time for our Australian families, as we await the trial’s commencement and children undergo the selection process. We are also mindful that this program is not applicable to all types of Sanfilippo. Please celebrate this historic milestone with us but keep all Sanfilippo families in your thoughts and prayers in the coming weeks.
In light of the exciting news about the Sanfilippo Type A Australian trial being underway, the fan club team wishes to congratulate the people of the Foundation, who's relentless pursuit of a chance at life for Sanfilippo children is tirelessly inspiring. As fans of Sébastien, who is an international ambassador for the Foundation since 2014, we reaffirm our commitment to stay by their side every step of the way!